Mucopolysaccharidosis type I Market Insights, Epidemiology and Market Forecasts, 2028: Focus on United States, EU5 (Germany, Spain, Italy, France and United Kingdom), and Japan
DUBLIN, Oct. 21, 2019 /PRNewswire/ -- The "Mucopolysaccharidosis type I Market Insights, Epidemiology and Market Forecast-2028" drug pipelines has been added to ResearchAndMarkets.com's offering.
This report delivers an in-depth understanding of the disease, historical & forecasted epidemiology as well as the market trends of MPS I in the United States, EU5 (Germany, Spain, Italy, France and United Kingdom), and Japan
The Report provides the current treatment practices, emerging drugs, market share of the individual therapies, current and forecasted market size of Mucopolysaccharidosis type I (MPS I) from 2017 to 2028 segmented by seven major markets. The Report also covers current treatment practice/algorithm practice market drivers, market barriers and unmet medical needs to curate best of the opportunities and assess underlying potential of the market
Mucopolysaccharidosis type I (MPS I) - Disease Understanding and Treatment Algorithm
The Mucopolysaccharidosis type I market report gives the thorough understanding of the Mucopolysaccharidosis type I by including details such as disease definition, classification, symptoms, etiology, pathophysiology, diagnostic trends. It also provides treatment algorithms and treatment guidelines for Mucopolysaccharidosis type I in the US, Europe, and Japan
Mucopolysaccharidosis type I Epidemiology
The Mucopolysaccharidosis type I epidemiology division provide the insights about historical and current patient pool and forecasted trend for every 7 major countries. It helps to recognize the causes of current and forecasted trends by exploring numerous studies and views of key opinion leaders. This part of The report also provides the diagnosed patient pool and their trends along with assumptions undertaken
The disease epidemiology covered in the report provides historical as well as forecasted epidemiology {total cases, Live Birth cases, overall prevalent cases, Severity Specific Cases [Hurler, Hurler-Scheie, Scheie] and diagnosed cases} scenario of Mucopolysaccharidosis type I in the 7MM covering United States, EU5 countries (Germany, Spain, Italy, France and United Kingdom) and Japan from 2017-2028
According to this research, total prevalent population of Mucopolysaccharidosis type I in 7 major markets was found to be 3,529 in 2017
Mucopolysaccharidosis type I Drug Chapters
This segment of the Mucopolysaccharidosis type I report encloses the detailed analysis of marketed drugs and late stage (Phase-III and Phase-II) pipeline drugs. It also helps to understand the clinical trial details, expressive pharmacological action, agreements and collaborations, approval and patent details, advantages and disadvantages of each included drug and the latest news and press releases
Mucopolysaccharidosis type I Market Outlook
The Mucopolysaccharidosis type I market outlook of the report helps to build the detailed comprehension of the historic, current and forecasted trend of the market by analyzing the impact of current therapies on the market, unmet needs, drivers and barriers and demand of better technology
According to this research, the market of Mucopolysaccharidosis type I in 7MM was found to be USD 333.31 million in 2017
Mucopolysaccharidosis type I Drugs Uptake
This section focusses on the rate of uptake of the potential drugs recently launched in the market or will get launched in the market during the study period from 2017-2028. The analysis covers market uptake by drugs; patient uptake by therapies and sales of each drug
Key Topics Covered:
1. Key Insights
2. Mucopolysaccharidosis type I (MPS I): Market Overview at a Glance
2.1. Total Market Share (%) Distribution of Mucopolysaccharidosis type I (MPS I) in 2017
2.2. Total Market Share (%) Distribution of Mucopolysaccharidosis type I (MPS I) in 2028
3. Mucopolysaccharidosis type I (MPS I): Disease Background and Overview
3.1. Introduction
3.2. Symptoms
3.3. Clinical Manifestations of MPS I
3.4. Severity Spectrum
3.5. Genetic Causes
3.6. Inheritance pattern
3.7. Pathophysiological mechanisms of MPS I
3.8. Diagnosis
3.8.1. Differential diagnosis
3.9. Newborn screening for MPS I
3.10. Challenges in predicting disease severity in newborn screening
3.11. Easy-to-use algorithm for faster diagnoses of MPS I
4. Epidemiology and Patient Population
4.1. Key Findings
5. Total Cases of Mucopolysaccharidosis type I in 7MM
6. United States Epidemiology
6.1. Assumptions and Rationale
6.2. Total cases of Mucopolysaccharidosis type I in the US
6.3. Live Birth Cases of Mucopolysaccharidosis type I in the United States
6.4. Overall Prevalent Cases of Mucopolysaccharidosis type I in the United States
6.5. Diagnosed Cases of MPS Type I in the United States
6.6. Severity Specific Cases of MPS Type I in the United States
7. EU5 Epidemiology
7.1. Germany Epidemiology
7.1.1. Total cases of Mucopolysaccharidosis type I in Germany
7.1.2. Live Birth Cases of Mucopolysaccharidosis type I in Germany
7.1.3. Overall Prevalent Cases of Mucopolysaccharidosis type I in Germany
7.1.4. Diagnosed Cases of MPS Type I in Germany
7.1.5. Severity Specific Cases of MPS Type I in Germany
7.2. France Epidemiology
7.3. Italy Epidemiology
7.4. Spain Epidemiology
7.5. United Kingdom Epidemiology
7.6. Japan Epidemiology
7.7. Assumptions and Rationale
7.8. Management and Treatment of MPS I
8. Unmet Needs
9. Marketed drugs
9.1. Aldurazyme: BioMarin Pharmaceutical/ Genzyme
9.1.1. Drug Description
9.1.2. Regulatory Milestones
9.1.3. Other Developmental Activities
9.1.4. Safety and Efficacy
9.1.5. Product Profile
10. Emerging Therapies
10.1. Key Cross Competition
10.2. MGTA-456: Magenta Therapeutics
10.2.1. Product Description
10.2.2. Other Developmental Activities
10.2.3. Clinical Development
10.2.4. Safety and Efficacy
10.2.5. Product Profile
10.3. Pentosan Polysulfate Sodium: Plexcera Therapeutics
10.4. Valanafusp alfa: Armagen
10.5. SB-318: Sangamo Therapeutics
11. Mucopolysaccharidosis type I (MPS I): 7MM Market Analysis
11.1. Key Findings
11.2. Market Size of Mucopolysaccharidosis type I in 7MM
12. United States: Market Outlook
13. EU-5 countries: Market Outlook
14. Japan Market Outlook
14.1. Japan Market Size
14.2. Total Market size of Mucopolysaccharidosis type I
14.3. Market Size of Mucopolysaccharidosis type I by Therapies in Japan
15. Market Drivers
16. Market Barriers
17. Appendix
Companies Mentioned
- ArmaGen
- Magenta Therapeutics
- Regenxbio
For more information about this drug pipelines report visit https://www.researchandmarkets.com/r/yv3nsv
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