Accessibility Statement Skip Navigation
  • Resources
  • Investor Relations
  • Journalists
  • Agencies
  • Client Login
  • Send a Release
Return to PR Newswire homepage
  • News
  • Products
  • Contact
When typing in this field, a list of search results will appear and be automatically updated as you type.

Searching for your content...

No results found. Please change your search terms and try again.
  • News in Focus
      • Browse News Releases

      • All News Releases
      • All Public Company
      • English-only
      • News Releases Overview

      • Multimedia Gallery

      • All Multimedia
      • All Photos
      • All Videos
      • Multimedia Gallery Overview

      • Trending Topics

      • All Trending Topics
  • Business & Money
      • Auto & Transportation

      • All Automotive & Transportation
      • Aerospace, Defense
      • Air Freight
      • Airlines & Aviation
      • Automotive
      • Maritime & Shipbuilding
      • Railroads and Intermodal Transportation
      • Supply Chain/Logistics
      • Transportation, Trucking & Railroad
      • Travel
      • Trucking and Road Transportation
      • Auto & Transportation Overview

      • View All Auto & Transportation

      • Business Technology

      • All Business Technology
      • Blockchain
      • Broadcast Tech
      • Computer & Electronics
      • Computer Hardware
      • Computer Software
      • Data Analytics
      • Electronic Commerce
      • Electronic Components
      • Electronic Design Automation
      • Financial Technology
      • High Tech Security
      • Internet Technology
      • Nanotechnology
      • Networks
      • Peripherals
      • Semiconductors
      • Business Technology Overview

      • View All Business Technology

      • Entertain­ment & Media

      • All Entertain­ment & Media
      • Advertising
      • Art
      • Books
      • Entertainment
      • Film and Motion Picture
      • Magazines
      • Music
      • Publishing & Information Services
      • Radio & Podcast
      • Television
      • Entertain­ment & Media Overview

      • View All Entertain­ment & Media

      • Financial Services & Investing

      • All Financial Services & Investing
      • Accounting News & Issues
      • Acquisitions, Mergers and Takeovers
      • Banking & Financial Services
      • Bankruptcy
      • Bond & Stock Ratings
      • Conference Call Announcements
      • Contracts
      • Cryptocurrency
      • Dividends
      • Earnings
      • Earnings Forecasts & Projections
      • Financing Agreements
      • Insurance
      • Investments Opinions
      • Joint Ventures
      • Mutual Funds
      • Private Placement
      • Real Estate
      • Restructuring & Recapitalization
      • Sales Reports
      • Shareholder Activism
      • Shareholder Meetings
      • Stock Offering
      • Stock Split
      • Venture Capital
      • Financial Services & Investing Overview

      • View All Financial Services & Investing

      • General Business

      • All General Business
      • Awards
      • Commercial Real Estate
      • Corporate Expansion
      • Earnings
      • Environmental, Social and Governance (ESG)
      • Human Resource & Workforce Management
      • Licensing
      • New Products & Services
      • Obituaries
      • Outsourcing Businesses
      • Overseas Real Estate (non-US)
      • Personnel Announcements
      • Real Estate Transactions
      • Residential Real Estate
      • Small Business Services
      • Socially Responsible Investing
      • Surveys, Polls and Research
      • Trade Show News
      • General Business Overview

      • View All General Business

  • Science & Tech
      • Consumer Technology

      • All Consumer Technology
      • Artificial Intelligence
      • Blockchain
      • Cloud Computing/Internet of Things
      • Computer Electronics
      • Computer Hardware
      • Computer Software
      • Consumer Electronics
      • Cryptocurrency
      • Data Analytics
      • Electronic Commerce
      • Electronic Gaming
      • Financial Technology
      • Mobile Entertainment
      • Multimedia & Internet
      • Peripherals
      • Social Media
      • STEM (Science, Tech, Engineering, Math)
      • Supply Chain/Logistics
      • Wireless Communications
      • Consumer Technology Overview

      • View All Consumer Technology

      • Energy & Natural Resources

      • All Energy
      • Alternative Energies
      • Chemical
      • Electrical Utilities
      • Gas
      • General Manufacturing
      • Mining
      • Mining & Metals
      • Oil & Energy
      • Oil and Gas Discoveries
      • Utilities
      • Water Utilities
      • Energy & Natural Resources Overview

      • View All Energy & Natural Resources

      • Environ­ment

      • All Environ­ment
      • Conservation & Recycling
      • Environmental Issues
      • Environmental Policy
      • Environmental Products & Services
      • Green Technology
      • Natural Disasters
      • Environ­ment Overview

      • View All Environ­ment

      • Heavy Industry & Manufacturing

      • All Heavy Industry & Manufacturing
      • Aerospace & Defense
      • Agriculture
      • Chemical
      • Construction & Building
      • General Manufacturing
      • HVAC (Heating, Ventilation and Air-Conditioning)
      • Machinery
      • Machine Tools, Metalworking and Metallurgy
      • Mining
      • Mining & Metals
      • Paper, Forest Products & Containers
      • Precious Metals
      • Textiles
      • Tobacco
      • Heavy Industry & Manufacturing Overview

      • View All Heavy Industry & Manufacturing

      • Telecomm­unications

      • All Telecomm­unications
      • Carriers and Services
      • Mobile Entertainment
      • Networks
      • Peripherals
      • Telecommunications Equipment
      • Telecommunications Industry
      • VoIP (Voice over Internet Protocol)
      • Wireless Communications
      • Telecomm­unications Overview

      • View All Telecomm­unications

  • Lifestyle & Health
      • Consumer Products & Retail

      • All Consumer Products & Retail
      • Animals & Pets
      • Beers, Wines and Spirits
      • Beverages
      • Bridal Services
      • Cannabis
      • Cosmetics and Personal Care
      • Fashion
      • Food & Beverages
      • Furniture and Furnishings
      • Home Improvement
      • Household, Consumer & Cosmetics
      • Household Products
      • Jewelry
      • Non-Alcoholic Beverages
      • Office Products
      • Organic Food
      • Product Recalls
      • Restaurants
      • Retail
      • Supermarkets
      • Toys
      • Consumer Products & Retail Overview

      • View All Consumer Products & Retail

      • Entertain­ment & Media

      • All Entertain­ment & Media
      • Advertising
      • Art
      • Books
      • Entertainment
      • Film and Motion Picture
      • Magazines
      • Music
      • Publishing & Information Services
      • Radio & Podcast
      • Television
      • Entertain­ment & Media Overview

      • View All Entertain­ment & Media

      • Health

      • All Health
      • Biometrics
      • Biotechnology
      • Clinical Trials & Medical Discoveries
      • Dentistry
      • FDA Approval
      • Fitness/Wellness
      • Health Care & Hospitals
      • Health Insurance
      • Infection Control
      • International Medical Approval
      • Medical Equipment
      • Medical Pharmaceuticals
      • Mental Health
      • Pharmaceuticals
      • Supplementary Medicine
      • Health Overview

      • View All Health

      • Sports

      • All Sports
      • General Sports
      • Outdoors, Camping & Hiking
      • Sporting Events
      • Sports Equipment & Accessories
      • Sports Overview

      • View All Sports

      • Travel

      • All Travel
      • Amusement Parks and Tourist Attractions
      • Gambling & Casinos
      • Hotels and Resorts
      • Leisure & Tourism
      • Outdoors, Camping & Hiking
      • Passenger Aviation
      • Travel Industry
      • Travel Overview

      • View All Travel

  • Policy & Public Interest
      • Policy & Public Interest

      • All Policy & Public Interest
      • Advocacy Group Opinion
      • Animal Welfare
      • Congressional & Presidential Campaigns
      • Corporate Social Responsibility
      • Domestic Policy
      • Economic News, Trends, Analysis
      • Education
      • Environmental
      • European Government
      • FDA Approval
      • Federal and State Legislation
      • Federal Executive Branch & Agency
      • Foreign Policy & International Affairs
      • Homeland Security
      • Labor & Union
      • Legal Issues
      • Natural Disasters
      • Not For Profit
      • Patent Law
      • Public Safety
      • Trade Policy
      • U.S. State Policy
      • Policy & Public Interest Overview

      • View All Policy & Public Interest

  • People & Culture
      • People & Culture

      • All People & Culture
      • Aboriginal, First Nations & Native American
      • African American
      • Asian American
      • Children
      • Diversity, Equity & Inclusion
      • Hispanic
      • Lesbian, Gay & Bisexual
      • Men's Interest
      • People with Disabilities
      • Religion
      • Senior Citizens
      • Veterans
      • Women
      • People & Culture Overview

      • View All People & Culture

      • In-Language News

      • Arabic
      • español
      • português
      • Česko
      • Danmark
      • Deutschland
      • España
      • France
      • Italia
      • Nederland
      • Norge
      • Polska
      • Portugal
      • Россия
      • Slovensko
      • Suomi
      • Sverige
  • Explore Our Platform
  • Plan Campaigns
  • Create with AI
  • Distribute Press Releases
  • Amplify Content
  • All Products
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices
  • Hamburger menu
  • PR Newswire: news distribution, targeting and monitoring
  • Send a Release
    • ALL CONTACT INFO
    • Contact Us

      888-776-0942
      from 8 AM - 10 PM ET

  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • News in Focus
    • Browse All News
    • Multimedia Gallery
    • Trending Topics
  • Business & Money
    • Auto & Transportation
    • Business Technology
    • Entertain­ment & Media
    • Financial Services & Investing
    • General Business
  • Science & Tech
    • Consumer Technology
    • Energy & Natural Resources
    • Environ­ment
    • Heavy Industry & Manufacturing
    • Telecomm­unications
  • Lifestyle & Health
    • Consumer Products & Retail
    • Entertain­ment & Media
    • Health
    • Sports
    • Travel
  • Policy & Public Interest
  • People & Culture
    • People & Culture
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • Explore Our Platform
  • Plan Campaigns
  • Create with AI
  • Distribute Press Releases
  • Amplify Content
  • All Products
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS

Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gaucher's and Niemann-Pick Poised to Supersede Existing Therapies


News provided by

Reportlinker

Mar 28, 2012, 04:23 ET

Share this article

Share toX

Share this article

Share toX

NEW YORK, March 28, 2012 /PRNewswire/ -- Reportlinker.com announces that a new market research report is available in its catalogue:

Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gaucher's and Niemann-Pick Poised to Supersede Existing Therapies

http://www.reportlinker.com/p0804701/Neurometabolic-Disorders-Market-to-2017---Novel-Therapies-for-Rare-Diseases-such-as-Gaucher's-and-Niemann-Pick-Poised-to-Supersede-Existing-Therapies.html#utm_source=prnewswire&utm_medium=pr&utm_campaign=Pathology

Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gaucher's and Niemann-Pick Poised to Supersede Existing Therapies

Summary

GBI Research has released its latest research, "Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gaucher's and Niemann-Pick Poised to Supersede Existing Therapies" which provides insights into global neurometabolic disorders market and market forecast until 2017. Report is built using data and information sourced from proprietary databases, primary and secondary research and in-house analysis by GBI Research's team of industry experts. The report provides an in-depth analysis of the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease. The report examines the treatment usage patterns and also includes insights into the R&D product pipeline and explores the competitive landscape including major players in neurometabolic disorders market. Finally, the report also includes analysis on Mergers and Acquisitions (M&As) and licensing agreements that took place in neurometabolic disorders market.

Scope

- The report analyzes market characterization, pipeline analysis and key M&A trends in the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease markets in the neurometabolic disorders market.

- Data and analysis on the contraceptives market in the leading geographies of the world – the US, the UK, Germany, France, Italy, Spain, and Japan.

- Annualized market data for the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease in the neurometabolic disorders market from 2002 to 2010, with forecasts to 2017.

- Market data on the therapeutic landscape which covers market revenues, treatment usage patterns and annual cost of therapy.

- Key drivers and restraints that have had a significant impact on the market

- The competitive landscape of the neurometabolic disorders market.

- Key M&A activities and Licensing Agreements that took place from 2005 to 2011 in the contraceptives market.

Reasons to buy

- Align your product portfolio to the markets with high growth potential.

- Develop market-entry and market expansion strategies by identifying the potential region and therapeutic segments poised for strong growth.

- Device a more tailored country strategy through the understanding of key drivers and barriers of the neurometabolic disorders market.

- Develop key strategic initiatives by understanding the key focus areas of leading companies.

- Accelerate and strengthen your market position by identifying key companies for mergers, acquisitions and strategic partnerships.

1 Table of Contents

1 Table of Contents 4

1.1 List of Tables 7

1.2 List of Figures 10

2 Neurometabolic Disorders Market to 2017 - Introduction 12

2.1 GBI Research Report Guidance 13

3 Neurometabolic Disorders Market to 2017 - Global Market Overview 14

3.1 Introduction 14

3.2 Market Revenue 14

3.3 Annual Cost of Therapy 16

3.3.1 Treatment Usage Pattern 17

4 Neurometabolic Disorders Market to 2017 - Geographical Landscape 20

4.1 The US 21

4.1.1 Revenue 21

4.1.2 Annual Cost of Therapy 23

4.1.3 Treatment Usage Pattern 24

4.2 Top Five Countries of Europe 26

4.2.1 Revenue 26

4.2.2 Annual Cost of Therapy 28

4.2.3 Treatment Usage Pattern 29

4.3 Japan 31

4.3.1 Revenue 31

4.3.2 Annual Cost of Therapy 32

4.3.3 Treatment Usage Pattern 33

5 Neurometabolic Disorders Market to 2017 - Therapeutic Landscape 35

5.1 Neurometabolic Disorders Market to 2017 - Gaucher's Disease 35

5.1.1 Introduction 35

5.1.2 Revenue 36

5.1.3 Revenue by Geography 38

5.1.4 Annual Cost of Therapy 40

5.1.5 Treatment Usage Pattern 41

5.1.6 Treatment Algorithm 43

5.1.7 Gaucher's Type 1 Disease Therapeutics Market Drivers 44

5.1.8 Gaucher's Type 1 Disease Therapeutics Market Restraints 45

5.2 Neurometabolic Disorders Market to 2017 - Niemann-Pick Type C Disease 45

5.2.1 Introduction 45

5.2.2 Revenue 47

5.2.3 Revenue by Geography 48

5.2.4 Annual Cost of Therapy 50

5.2.5 Treatment Usage Pattern 51

5.2.6 Treatment Algorithm 53

5.2.7 Niemann-Pick Type C Market Drivers 54

5.2.8 Niemann-Pick Type C Market Restraints 55

5.3 Neurometabolic Disorders Market to 2017 - Pompe Disease 56

5.3.1 Introduction 56

5.3.2 Revenue 56

5.3.3 Revenue by Geography 58

5.3.4 Annual Cost of Therapy 60

5.3.5 Treatment Usage Pattern 61

5.3.6 Treatment Algorithm 63

5.3.7 Pompe Disease Therapeutics Market Drivers 64

5.3.8 Pompe Disease Therapeutics Market Restraints 65

5.4 Neurometabolic Disorders Market to 2017 - Fabry Disease 65

5.4.1 Introduction 65

5.4.2 Revenue 65

5.4.3 Revenue by Geography 67

5.4.4 Annual Cost of Therapy 69

5.4.5 Treatment Usage Pattern 70

5.4.6 Fabry Disease Therapeutics Market Drivers 72

5.4.7 Fabry Disease Therapeutics Market Restraints 73

5.5 Neurometabolic Disorders Market to 2017 - Mucopolysaccharidosis VI 73

5.5.1 Introduction 73

5.5.2 Revenue 74

5.5.3 Revenue by Geography 75

5.5.4 Annual Cost of Therapy 76

5.5.5 Treatment Usage Pattern 77

5.5.6 Treatment Algorithm 79

5.5.7 Mucopolysaccharidosis VI Therapeutics Market Drivers 80

5.5.8 Mucopolysaccharidosis VI Therapeutics Market Restraints 81

6 Neurometabolic Disorders Market to 2017 - Major Marketed Products 82

6.1 Gaucher's Disease 82

6.1.1 Cerezyme 82

6.1.2 VPRIV 83

6.2 Gaucher's Disease and Niemann-Pick Type C 85

6.2.1 Zavesca 85

6.3 Pompe Disease 86

6.3.1 Myozyme/Lumizyme 86

6.4 Fabry Disease 88

6.4.1 Fabrazyme 88

6.4.2 Replagal 89

6.5 Mucopolysaccharidosis VI 91

6.5.1 Naglazyme 91

7 Neurometabolic Disorders Market to 2017 - Product Pipeline Analysis 92

7.1 Gaucher's Disease - Research and Development Pipeline 94

7.1.1 Overview 94

7.1.2 Pipeline by Phase 94

7.2 Niemann-Pick Type C: Research and Development Pipeline 95

7.2.1 Overview 95

7.2.2 Pipeline by Phase 95

7.3 Pompe Disease: Research and Development Pipeline 96

7.3.1 Overview 96

7.3.2 Pipeline by Phase 96

7.4 Fabry Disease: Research and Development Pipeline 97

7.4.1 Overview 97

7.4.2 Pipeline by Phase 97

7.5 Most Promising Molecules 98

7.5.1 Uplyso 98

7.5.2 Genz-112638 99

7.5.3 Amigal 101

8 Neurometabolic Disorders Market to 2017- Competitive Landscape 103

8.1 Overview 103

8.2 Company Profiles 105

8.2.1 Genzyme Corporation 105

8.2.2 Shire 113

8.2.3 BioMarin Pharmaceutical Inc. 120

8.2.4 Actelion 124

9 Neurometabolic Disorders Market to 2017 - Strategic Consolidations 128

9.1 Overview 128

9.1.1 Sanofi S.A. Completes Acquisition of Genzyme 129

9.1.2 Pfizer Enters into a Licensing Agreement with Protalix Biotherapeutics 130

9.1.3 GlaxoSmithKline Enters into Licensing Agreement with Amicus Therapeutics for Amigal 130

9.1.4 Amicus Therapeutics Terminates Licensing Agreement with Shire 131

9.2 Deals by Geography 131

9.3 Deals by Licensing Type 132

9.4 Deals by Value 133

9.5 Deals by Phase 134

9.5.1 NDA Filed 134

9.5.2 Phase III 134

10 Neurometabolic Disorders Market to 2017 - Appendix 135

10.1 Market Definitions 135

10.2 Abbreviations 135

10.3 Research Methodology 136

10.3.1 Coverage 136

10.3.2 Secondary Research 137

10.3.3 Primary Research 137

10.4 Therapeutic Landscape 138

10.4.2 Market Size by Geography 140

10.5 Geographical Landscape 141

10.6 Pipeline Analysis 141

10.7 Competitive Landscape 141

10.7.1 Expert Panel Validation 141

10.8 Contact Us 141

10.9 Disclaimer 141

10.10 Sources 142

1.1 List of Tables

Table 1: Neurometabolic Disorders Market to 2017, Global, Revenue ($m), 2002-2010 15

Table 2: Neurometabolic Disorders Market to 2017, Global, Revenue Forecasts ($m), 2010-2017 15

Table 3: Neurometabolic Disorders Market to 2017, Global, Annual Cost of Therapy ($), 2002-2010 16

Table 4: Neurometabolic Disorders Market to 2017, Global, Annual Cost of Therapy ($), 2010-2017 16

Table 5: Neurometabolic Disorders Market to 2017, Global, Treatment Usage Pattern, 2002-2010 17

Table 6: Neurometabolic Disorders Market to 2017, Global, Treatment Usage Pattern, 2010-2017 18

Table 7: Neurometabolic Disorders Market to 2017, Global, Revenue, By Geography ($m), 2002-2010 20

Table 8: Neurometabolic Disorders Market to 2017, Global, Revenue Forecasts, By Geography ($m), 2010-2017 21

Table 9: Neurometabolic Disorders Market to 2017, The US, Revenue ($m), 2002-2010 22

Table 10: Neurometabolic Disorders Market to 2017, The US, Revenue Forecasts ($m), 2010-2017 22

Table 11: Neurometabolic Disorders Market to 2017, The US, Annual Cost of Therapy ($), 2002-2010 23

Table 12: Neurometabolic Disorders Market to 2017, The US, Annual Cost of Therapy ($), 2010-2017 24

Table 13: Neurometabolic Disorders Market to 2017, The US, Treatment Usage Pattern, 2002-2010 25

Table 14: Neurometabolic Disorders Market to 2017, The US, Treatment Usage Pattern, 2010-2017 25

Table 15: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Revenue ($m) 2002-2010 27

Table 16: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Revenue Forecasts ($m), 2010-2017 27

Table 17: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Annual Cost of Therapy ($), 2002-2010 28

Table 18: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Annual Cost of Therapy ($), 2010-2017 28

Table 19: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Treatment Usage Pattern, 2002-2010 29

Table 20: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Treatment Usage Pattern, 2010-2017 30

Table 21: Neurometabolic Disorders Market to 2017, Japan, Revenue ($m), 2002-2010 31

Table 22: Neurometabolic Disorders Market to 2017, Japan, Revenue Forecasts ($m), 2010-2017 32

Table 23: Neurometabolic Disorders Market to 2017, Japan, Annual Cost of Therapy ($), 2002-2010 32

Table 24: Neurometabolic Disorders Market to 2017, Japan, Annual Cost of Therapy ($), 2010-2017 33

Table 25: Neurometabolic Disorders Market to 2017, Japan, Treatment Usage Pattern, 2002-2010 34

Table 26: Neurometabolic Disorders Market to 2017, Japan, Treatment Usage Pattern, 2010-2017 34

Table 27: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue ($m), 2002-2010 36

Table 28: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue Forecasts ($m), 2010-2017 36

Table 29: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue, By Geography ($m), 2002-2010 38

Table 30: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue Forecasts, By Geography ($m), 2010-2017 39

Table 31: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Annual Cost of Therapy ($), 2002-2010 40

Table 32: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Annual Cost of Therapy ($), 2010-2017 40

Table 33: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Treatment Usage Pattern, 2002-2010 41

Table 34: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Treatment Usage Pattern, 2010-2017 42

Table 35: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue ($m), 2002-2010 47

Table 36: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue Forecasts ($m), 2010-2017 47

Table 37: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue, By Geography ($m), 2002-2010 49

Table 38: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue Forecasts, By Geography ($m), 2010-2017 49

Table 39: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Annual Cost of Therapy ($), 2009-2017 50

Table 40: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Treatment Usage Pattern, 2002-2010 51

Table 41: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Treatment Usage Pattern, 2010-2017 52

Table 42: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue ($m), 2002-2010 57

Table 43: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue Forecasts ($m), 2010-2017 57

Table 44: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue, By Geography ($m), 2002-2010 59

Table 45: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue Forecasts, By Geography ($m), 2010-2017 59

Table 46: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Annual Cost of Therapy ($), 2002-2010 60

Table 47: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Annual Cost of Therapy ($), 2010-2017 61

Table 48: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Treatment Usage Pattern, 2002-2010 62

Table 49: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Treatment Usage Pattern, 2010-2017 62

Table 50: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue ($m), 2002-2010 66

Table 51: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue Forecasts ($m), 2010-2017 66

Table 52: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue, By Geography ($m), 2002-2010 68

Table 53: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue Forecasts, By Geography ($m), 2010-2017 68

Table 54: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Annual Cost of Therapy ($), 2002-2010 69

Table 55: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Annual Cost of Therapy ($), 2010-2017 69

Table 56: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Treatment Usage Pattern, 2002-2010 70

Table 57: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Treatment Usage Pattern, 2010-2017 71

Table 58: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue ($m), 2002-2010 74

Table 59: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue Forecasts ($m), 2010-2017 74

Table 60: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue, By Geography ($m), 2002-2010 75

Table 61: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue Forecasts, By Geography ($m), 2010-2017 76

Table 62: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Annual Cost of Therapy ($), 2002-2010 76

Table 63: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Annual Cost of Therapy ($), 2010-2017 77

Table 64: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Treatment Usage Pattern, 2002-2010 77

Table 65: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Treatment Usage Pattern, 2010-2017 78

Table 66: Neurometabolic Disorders Market to 2017, Global, Major Marketed Products, 2010 82

Table 67: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Pipeline by Phase, 2011 94

Table 68: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Pipeline by Phase, 2011 95

Table 69: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Pipeline by Phase, 2011 96

Table 70: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Pipeline by Phase, 2011 97

Table 71: Neurometabolic Disorders Market to 2017, Global, Pipeline, Most Promising Molecules, 2011 98

Table 72: Neurometabolic Disorders Market to 2017, Global, Major Marketed Products, 2010 104

Table 73: Neurometabolic Disorders Market to 2017, Global, Genzyme Corporation, Major Deals, 2004-2011 106

Table 74: Neurometabolic Disorders Market to 2017, Global, Shire plc, Major Deals, 2004-2011 114

Table 75: Neurometabolic Disorders Market to 2017, Global, BioMarin Pharmaceutical Inc., Major Deals, 2004-2011 122

Table 76: Neurometabolic Disorders Market to 2017, Global, Actelion Ltd., Major Deals, 2004-2011 126

Table 77: Neurometabolic Disorders Market to 2017, Global, Comparison of Therapy Areas under Drug Development and Research, 2011 129

Table 78: Neurometabolic Disorders Market to 2017, Global, Genzyme Corporation, Late-stage Pipeline, 2011 130

1.2 List of Figures

Figure 1: Neurometabolic Disorders Market to 2017, Global, Revenue Forecasts ($m), 2002-2017 15

Figure 2: Neurometabolic Disorders Market to 2017, Global, Annual Cost of Therapy ($), 2002-2017 16

Figure 3: Neurometabolic Disorders Market to 2017, Global, Treatment Usage Pattern, 2002-2017 17

Figure 4: Neurometabolic Disorders Market to 2017, Global, Revenue Forecasts, By Geography ($m), 2002-2017 20

Figure 5: Neurometabolic Disorders Market to 2017, The US, Revenue Forecasts ($m), 2002-2017 22

Figure 6: Neurometabolic Disorders Market to 2017, The US, Annual Cost of Therapy ($), 2002-2017 23

Figure 7: Neurometabolic Disorders Market to 2017, The US, Treatment Usage Pattern, 2002-2017 24

Figure 8: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Revenue Forecasts ($m), 2002-2017 27

Figure 9: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Annual Cost of Therapy ($), 2002-2017 28

Figure 10: Neurometabolic Disorders Market to 2017, Top Five Countries of Europe, Treatment Usage Pattern, 2002-2017 29

Figure 11: Neurometabolic Disorders Market to 2017, Japan, Revenue Forecasts ($m), 2002-2017 31

Figure 12: Neurometabolic Disorders Market to 2017, Japan, Annual Cost of Therapy ($), 2002-2017 32

Figure 13: Neurometabolic Disorders Market to 2017, Japan, Treatment Usage Pattern, 2002-2017 33

Figure 14: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue Forecasts ($m), 2002-2017 36

Figure 15: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Revenue Forecasts, By Geography ($m), 2002-2017 38

Figure 16: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Annual Cost of Therapy ($), 2002-2017 40

Figure 17: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Treatment Usage Pattern, 2002-2017 41

Figure 18: Neurometabolic Disorders Market to 2017, Gaucher's Disease, Treatment Algorithm, 2011 43

Figure 19: Neurometabolic Disorders Market to 2017, Gaucher's Disease, Drivers and Restraints, 2011 44

Figure 20: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue Forecasts ($m), 2009-2017 47

Figure 21: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Revenue Forecasts, By Geography ($m), 2009-2017 49

Figure 22: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Annual Cost of Therapy ($), 2009-2017 50

Figure 23: Neurometabolic Disorders Market to 2017, Global, Niemann-Pick Type C, Treatment Usage Pattern, 2002-2017 51

Figure 24: Neurometabolic Disorders Market to 2017, Niemann-Pick Type C, Treatment Algorithm, 2011 53

Figure 25: Neurometabolic Disorders Market to 2017, Niemann-Pick Type C, Drivers and Restraints, 2011 54

Figure 26: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue Forecasts ($m), 2006-2017 56

Figure 27: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Revenue Forecasts, By Geography ($m), 2006-2017 58

Figure 28: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Annual Cost of Therapy ($), 2006-2017 60

Figure 29: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Treatment Usage Pattern, 2002-2017 61

Figure 30: Neurometabolic Disorders Market to 2017, Pompe Disease, Treatment Algorithm, 2011 63

Figure 31: Neurometabolic Disorders Market to 2017, Pompe Disease, Drivers and Restraints, 2011 64

Figure 32: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue Forecasts ($m), 2002-2017 66

Figure 33: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Revenue Forecasts, By Geography ($m), 2002-2017 67

Figure 34: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Annual Cost of Therapy ($), 2002-2017 69

Figure 35: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Treatment Usage Pattern, 2002-2017 70

Figure 36: Neurometabolic Disorders Market to 2017, Fabry Disease, Drivers and Restraints, 2011 72

Figure 37: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue Forecasts ($m), 2005-2017 74

Figure 38: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Revenue Forecasts, By Geography ($m), 2005-2017 75

Figure 39: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Annual Cost of Therapy ($), 2005-2017 76

Figure 40: Neurometabolic Disorders Market to 2017, Global, Mucopolysaccharidosis VI, Treatment Usage Pattern, 2002-2017 77

Figure 41: Neurometabolic Disorders Market to 2017, Mucopolysaccharidosis VI, Treatment Algorithm, 2011 79

Figure 42: Neurometabolic Disorders Market to 2017, Mucopolysaccharidosis VI, Drivers and Restraints, 2011 80

Figure 43: Neurometabolic Disorders Market to 2017, Global, Pipeline by Phase, 2011 92

Figure 44: Neurometabolic Disorders Market to 2017, Global, Pipeline by Indication, 2011 93

Figure 45: Neurometabolic Disorders Market to 2017, Global, Gaucher's Disease, Pipeline by Phase, 2011 94

Figure 46: Neurometabolic Disorders Market to 2017, Global, Pompe Disease, Pipeline by Phase, 2011 96

Figure 47: Neurometabolic Disorders Market to 2017, Global, Fabry Disease, Pipeline by Phase, 2011 97

Figure 48: Neurometabolic Disorders Market to 2017, Global, Competitive Landscape (%), 2010 103

Figure 49: Neurometabolic Disorders Market to 2017, Global, Competitive Analysis of Top Four Players, Market Share and CAGR (%), 2008-2010 104

Figure 50: Neurometabolic Disorders Market to 2017, Global, Genzyme Corporation, SWOT Analysis, 2010 105

Figure 51: Neurometabolic Disorders Market to 2017, Global, Shire plc, SWOT Analysis, 2010 113

Figure 52: Neurometabolic Disorders Market to 2017, Global, BioMarin Pharmaceutical Inc., SWOT Analysis, 2010 121

Figure 53: Neurometabolic Disorders Market to 2017, Global, Actelion Ltd., SWOT Analysis, 2010 125

Figure 54: Neurometabolic Disorders Market to 2017, Global, Deals by Indication (%), 2011 128

Figure 55: Neurometabolic Disorders Market to 2017, Global, Deals by Geography (%), 2004-2011 131

Figure 56: Neurometabolic Disorders Market to 2017, Global, Deals by Type (%), 2004-2011 132

Figure 57: Neurometabolic Disorders Market to 2017, Global, Deals by Value (%), 2004-2011 133

Figure 58: Neurometabolic Disorders Market to 2017, Global, Deals by Phase (%), 2004-2011 134

Figure 59: GBI Research Market Forecasting Model 140

Companies mentioned

Genzyme Corporation

Shire

BioMarin Pharmaceutical Inc.

Actelion

To order this report:

Pathology Industry: Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gaucher's and Niemann-Pick Poised to Supersede Existing Therapies

More  Market Research Report

Check our  Industry Analysis and Insights

CONTACT:
Nicolas Bombourg
Reportlinker
Email: [email protected]
US: (805)652-2626
Intl: +1 805-652-2626

SOURCE Reportlinker

WANT YOUR COMPANY'S NEWS FEATURED ON PRNEWSWIRE.COM?

icon3
440k+
Newsrooms &
Influencers
icon1
9k+
Digital Media
Outlets
icon2
270k+
Journalists
Opted In
GET STARTED

Modal title

Contact PR Newswire

  • Call PR Newswire at 888-776-0942
    from 8 AM - 9 PM ET
  • Chat with an Expert
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices

Products

  • For Marketers
  • For Public Relations
  • For IR & Compliance
  • For Agency
  • All Products

About

  • About PR Newswire
  • About Cision
  • Become a Publishing Partner
  • Become a Channel Partner
  • Careers
  • Accessibility Statement
  • APAC
  • APAC - Simplified Chinese
  • APAC - Traditional Chinese
  • Brazil
  • Canada
  • Czech
  • Denmark
  • Finland
  • France
  • Germany
  • India
  • Indonesia
  • Israel
  • Italy
  • Japan
  • Korea
  • Mexico
  • Middle East
  • Middle East - Arabic
  • Netherlands
  • Norway
  • Poland
  • Portugal
  • Russia
  • Slovakia
  • Spain
  • Sweden
  • United Kingdom
  • Vietnam

My Services

  • All New Releases
  • Platform Login
  • ProfNet
  • Data Privacy

Do not sell or share my personal information:

  • Submit via [email protected] 
  • Call Privacy toll-free: 877-297-8921

Contact PR Newswire

Products

About

My Services
  • All News Releases
  • Platform Login
  • ProfNet
Call PR Newswire at
888-776-0942
  • Terms of Use
  • Privacy Policy
  • Information Security Policy
  • Site Map
  • RSS
  • Cookies
Copyright © 2025 Cision US Inc.