REGENXBIO to Present Interim Phase I/IIa Trial Update for RGX-314 for the Treatment of Wet AMD at the American Academy of Ophthalmology 2019 Annual Meeting in October

ROCKVILLE, Md., Aug. 27, 2019 /PRNewswire/ -- REGENXBIO Inc. (Nasdaq: RGNX), a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy based on its proprietary NAV^® Technology Platform, today announced that an interim trial update from the RGX-314 Phase I/IIa clinical trial for the treatment of wet age-related macular degeneration (wet AMD) will be reported during a presentation at the Retina Subspecialty Day program of the American Academy of Ophthalmology (AAO) 2019 Annual Meeting in San Francisco, CA. The results will be presented by Dr. Jeffrey S. Heier, M.D., Co-President and Director of Retina Research at Ophthalmic Consultants of Boston, and primary investigator for the trial. Dr. Heier will present the interim results that include data for all five dose cohorts. 

"We are excited by the previously announced positive interim data from the Phase I/IIa RGX-314 trial and the potential of NAV gene therapy as a one-time treatment for wet AMD, and we look forward to the presentation of data from all five dose cohorts from the Phase I/IIa clinical trial in wet AMD at the upcoming AAO meeting," said Steve Pakola, M.D., Senior Vice President and Chief Medical Officer of REGENXBIO.

Details of the presentation are as follows:

Title: Results of Cohorts 1-5 for the RGX-314 Phase I/IIa Study of Gene Therapy for Neovascular wAMD
Presenter: Jeffrey S. Heier, M.D., Co-President and Director of Retina Research at Ophthalmic Consultants of Boston
Session date/time: Friday, October 11, 2019, 4:18 p.m. PT / 7:18 p.m. ET
Session title: RET11 – Section VIII: Late Breaking Developments, Part 1
Room: Moscone Center, WEST 3002

About REGENXBIO Inc.

REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy. REGENXBIO's NAV Technology Platform, a proprietary adeno-associated virus (AAV) gene delivery platform, consists of exclusive rights to more than 100 novel AAV vectors, including AAV7, AAV8, AAV9 and AAVrh10. REGENXBIO and its third-party NAV Technology Platform Licensees are applying the NAV Technology Platform in the development of a broad pipeline of candidates in multiple therapeutic areas.

Forward-Looking Statements

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Contacts:

Investors:
Heather Savelle, 212-600-1902
[email protected]

Media:
David Rosen, 212-600-1902
[email protected]

SOURCE REGENXBIO Inc.