SOM Biotech is Launching an Indiegogo Crowdfunding Campaign for Pediatric Rare Diseases

SOM Biotech seeks to raise at least $300,000 for new initiative to investigate therapeutic options for pediatric rare diseases Cystic Fibrosis, Duchenne Muscular Dystrophy, Gaucher Disease, Niemann Pick Disease Type C, and Osteogenesis Imperfecta.

Dec 16, 2015, 08:35 ET from SOM Biotech

BARCELONA, Spain, Dec. 16, 2015 /PRNewswire/ -- SOM Biotech, with headquarters located at the Barcelona Science Park (PCB), is announcing its very first crowdfunding campaign for the purpose of initiating new R&D projects, related to pediatric rare diseases field. The diseases to be investigated are Cystic Fibrosis, Duchenne Muscular Dystrophy, Gaucher Disease, Niemann Pick Disease Type C, and Osteogenesis Imperfecta. The company plans to raise at least 300,000 $USD, which would be divided evenly among the five different pediatric rare diseases.

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Crowdfunding & New Initiative in Pediatric Rare Diseases

Recently, SOM Biotech has completed a Phase IIa clinical trial for Transthyretin Amyloidosis (ATTR) with successful results. Optimistic results obtained from this study, along with another clinical program in Huntington's Disease, were primary motivations in starting this new initiative. In addition, almost 50% of rare disease patients worldwide are children. Pediatric rare diseases with ongoing unmet needs include:

  1. Cystic Fibrosis
  2. Duchenne Muscular Dystrophy
  3. Gaucher Disease
  4. Niemann Pick Disease Type C
  5. Osteogenesis Imperfecta

With the aspirational goal of raising at least 300,000 $USD, funding will be used to investigate new therapeutic options for these 5 pediatric rare diseases. The amount will be allocated evenly to each pediatric rare disease program, funding the initial stages of drug repurposing identification to reach the clinical stages of development. At present a list of reference compounds for each pediatric rare disease program has been internally generated and scientifically-evaluated, with plans of identifying new and better therapeutic candidates. SOM's commitment is to advance further in the development of any promising drug to reach the market as soon as possible.

The Crowdfunding campaign takes place within a 2-month period starting from December 3rd, 2015, and will end on February 2ndst, 2016. The chosen platform is the American-based, yet globally-exposed, Indiegogo where funding for all campaigns can be made from public rewards-based donations. Through there SOM Biotech's campaign will be visible worldwide to various individuals and communities, interested in making a difference for pediatric rare diseases. Given the successes of its clinical programs and the support provided by various organizations, including the Spanish Federation of Rare Diseases (FEDER), senior management is confident of an outstanding performance and the pursuit of long-desired projects.

About SOM Biotech 

SOM Biotech Ltd. ( is a clinical-stage biopharmaceutical company based within the Barcelona Science Park, founded in 2009. The company's mission is to conduct drug identification, experimental demonstration, intellectual protection, clinical proof-of-concept and licensing of new applications and medical indications for previously marketed drugs (repositioning or reprofiling). Identification is performed using a proprietary computational virtual screening platform. SOM has an extensive pipeline of products under development ranging from rare diseases (TTR amyloidosis, Huntington's disease and glioblastoma) to other therapeutic areas (Alzheimer's disease and benign prostatic hyperplasia).

For further information:

Please visit our Indiegogo campaign page:

Alternatively, inquiries can be submitted to:

Press contact:
Beatriz Beltran
Tech Sales Comunicacion - Gabinete de Prensa
Tel.: + 34 93 303 22 70