Accessibility Statement Skip Navigation
  • Resources
  • Investor Relations
  • Journalists
  • Agencies
  • Client Login
  • Send a Release
Return to PR Newswire homepage
  • News
  • Products
  • Contact
When typing in this field, a list of search results will appear and be automatically updated as you type.

Searching for your content...

No results found. Please change your search terms and try again.
  • News in Focus
      • Browse News Releases

      • All News Releases
      • All Public Company
      • English-only
      • News Releases Overview

      • Multimedia Gallery

      • All Multimedia
      • All Photos
      • All Videos
      • Multimedia Gallery Overview

      • Trending Topics

      • All Trending Topics
  • Business & Money
      • Auto & Transportation

      • All Automotive & Transportation
      • Aerospace, Defense
      • Air Freight
      • Airlines & Aviation
      • Automotive
      • Maritime & Shipbuilding
      • Railroads and Intermodal Transportation
      • Supply Chain/Logistics
      • Transportation, Trucking & Railroad
      • Travel
      • Trucking and Road Transportation
      • Auto & Transportation Overview

      • View All Auto & Transportation

      • Business Technology

      • All Business Technology
      • Blockchain
      • Broadcast Tech
      • Computer & Electronics
      • Computer Hardware
      • Computer Software
      • Data Analytics
      • Electronic Commerce
      • Electronic Components
      • Electronic Design Automation
      • Financial Technology
      • High Tech Security
      • Internet Technology
      • Nanotechnology
      • Networks
      • Peripherals
      • Semiconductors
      • Business Technology Overview

      • View All Business Technology

      • Entertain­ment & Media

      • All Entertain­ment & Media
      • Advertising
      • Art
      • Books
      • Entertainment
      • Film and Motion Picture
      • Magazines
      • Music
      • Publishing & Information Services
      • Radio & Podcast
      • Television
      • Entertain­ment & Media Overview

      • View All Entertain­ment & Media

      • Financial Services & Investing

      • All Financial Services & Investing
      • Accounting News & Issues
      • Acquisitions, Mergers and Takeovers
      • Banking & Financial Services
      • Bankruptcy
      • Bond & Stock Ratings
      • Conference Call Announcements
      • Contracts
      • Cryptocurrency
      • Dividends
      • Earnings
      • Earnings Forecasts & Projections
      • Financing Agreements
      • Insurance
      • Investments Opinions
      • Joint Ventures
      • Mutual Funds
      • Private Placement
      • Real Estate
      • Restructuring & Recapitalization
      • Sales Reports
      • Shareholder Activism
      • Shareholder Meetings
      • Stock Offering
      • Stock Split
      • Venture Capital
      • Financial Services & Investing Overview

      • View All Financial Services & Investing

      • General Business

      • All General Business
      • Awards
      • Commercial Real Estate
      • Corporate Expansion
      • Earnings
      • Environmental, Social and Governance (ESG)
      • Human Resource & Workforce Management
      • Licensing
      • New Products & Services
      • Obituaries
      • Outsourcing Businesses
      • Overseas Real Estate (non-US)
      • Personnel Announcements
      • Real Estate Transactions
      • Residential Real Estate
      • Small Business Services
      • Socially Responsible Investing
      • Surveys, Polls and Research
      • Trade Show News
      • General Business Overview

      • View All General Business

  • Science & Tech
      • Consumer Technology

      • All Consumer Technology
      • Artificial Intelligence
      • Blockchain
      • Cloud Computing/Internet of Things
      • Computer Electronics
      • Computer Hardware
      • Computer Software
      • Consumer Electronics
      • Cryptocurrency
      • Data Analytics
      • Electronic Commerce
      • Electronic Gaming
      • Financial Technology
      • Mobile Entertainment
      • Multimedia & Internet
      • Peripherals
      • Social Media
      • STEM (Science, Tech, Engineering, Math)
      • Supply Chain/Logistics
      • Wireless Communications
      • Consumer Technology Overview

      • View All Consumer Technology

      • Energy & Natural Resources

      • All Energy
      • Alternative Energies
      • Chemical
      • Electrical Utilities
      • Gas
      • General Manufacturing
      • Mining
      • Mining & Metals
      • Oil & Energy
      • Oil and Gas Discoveries
      • Utilities
      • Water Utilities
      • Energy & Natural Resources Overview

      • View All Energy & Natural Resources

      • Environ­ment

      • All Environ­ment
      • Conservation & Recycling
      • Environmental Issues
      • Environmental Policy
      • Environmental Products & Services
      • Green Technology
      • Natural Disasters
      • Environ­ment Overview

      • View All Environ­ment

      • Heavy Industry & Manufacturing

      • All Heavy Industry & Manufacturing
      • Aerospace & Defense
      • Agriculture
      • Chemical
      • Construction & Building
      • General Manufacturing
      • HVAC (Heating, Ventilation and Air-Conditioning)
      • Machinery
      • Machine Tools, Metalworking and Metallurgy
      • Mining
      • Mining & Metals
      • Paper, Forest Products & Containers
      • Precious Metals
      • Textiles
      • Tobacco
      • Heavy Industry & Manufacturing Overview

      • View All Heavy Industry & Manufacturing

      • Telecomm­unications

      • All Telecomm­unications
      • Carriers and Services
      • Mobile Entertainment
      • Networks
      • Peripherals
      • Telecommunications Equipment
      • Telecommunications Industry
      • VoIP (Voice over Internet Protocol)
      • Wireless Communications
      • Telecomm­unications Overview

      • View All Telecomm­unications

  • Lifestyle & Health
      • Consumer Products & Retail

      • All Consumer Products & Retail
      • Animals & Pets
      • Beers, Wines and Spirits
      • Beverages
      • Bridal Services
      • Cannabis
      • Cosmetics and Personal Care
      • Fashion
      • Food & Beverages
      • Furniture and Furnishings
      • Home Improvement
      • Household, Consumer & Cosmetics
      • Household Products
      • Jewelry
      • Non-Alcoholic Beverages
      • Office Products
      • Organic Food
      • Product Recalls
      • Restaurants
      • Retail
      • Supermarkets
      • Toys
      • Consumer Products & Retail Overview

      • View All Consumer Products & Retail

      • Entertain­ment & Media

      • All Entertain­ment & Media
      • Advertising
      • Art
      • Books
      • Entertainment
      • Film and Motion Picture
      • Magazines
      • Music
      • Publishing & Information Services
      • Radio & Podcast
      • Television
      • Entertain­ment & Media Overview

      • View All Entertain­ment & Media

      • Health

      • All Health
      • Biometrics
      • Biotechnology
      • Clinical Trials & Medical Discoveries
      • Dentistry
      • FDA Approval
      • Fitness/Wellness
      • Health Care & Hospitals
      • Health Insurance
      • Infection Control
      • International Medical Approval
      • Medical Equipment
      • Medical Pharmaceuticals
      • Mental Health
      • Pharmaceuticals
      • Supplementary Medicine
      • Health Overview

      • View All Health

      • Sports

      • All Sports
      • General Sports
      • Outdoors, Camping & Hiking
      • Sporting Events
      • Sports Equipment & Accessories
      • Sports Overview

      • View All Sports

      • Travel

      • All Travel
      • Amusement Parks and Tourist Attractions
      • Gambling & Casinos
      • Hotels and Resorts
      • Leisure & Tourism
      • Outdoors, Camping & Hiking
      • Passenger Aviation
      • Travel Industry
      • Travel Overview

      • View All Travel

  • Policy & Public Interest
      • Policy & Public Interest

      • All Policy & Public Interest
      • Advocacy Group Opinion
      • Animal Welfare
      • Congressional & Presidential Campaigns
      • Corporate Social Responsibility
      • Domestic Policy
      • Economic News, Trends, Analysis
      • Education
      • Environmental
      • European Government
      • FDA Approval
      • Federal and State Legislation
      • Federal Executive Branch & Agency
      • Foreign Policy & International Affairs
      • Homeland Security
      • Labor & Union
      • Legal Issues
      • Natural Disasters
      • Not For Profit
      • Patent Law
      • Public Safety
      • Trade Policy
      • U.S. State Policy
      • Policy & Public Interest Overview

      • View All Policy & Public Interest

  • People & Culture
      • People & Culture

      • All People & Culture
      • Aboriginal, First Nations & Native American
      • African American
      • Asian American
      • Children
      • Diversity, Equity & Inclusion
      • Hispanic
      • Lesbian, Gay & Bisexual
      • Men's Interest
      • People with Disabilities
      • Religion
      • Senior Citizens
      • Veterans
      • Women
      • People & Culture Overview

      • View All People & Culture

      • In-Language News

      • Arabic
      • español
      • português
      • Česko
      • Danmark
      • Deutschland
      • España
      • France
      • Italia
      • Nederland
      • Norge
      • Polska
      • Portugal
      • Россия
      • Slovensko
      • Suomi
      • Sverige
  • Explore Our Platform
  • Plan Campaigns
  • Create with AI
  • Distribute Press Releases
  • Amplify Content
  • All Products
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices
  • Hamburger menu
  • PR Newswire: news distribution, targeting and monitoring
  • Send a Release
    • ALL CONTACT INFO
    • Contact Us

      888-776-0942
      from 8 AM - 10 PM ET

  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • News in Focus
    • Browse All News
    • Multimedia Gallery
    • Trending Topics
  • Business & Money
    • Auto & Transportation
    • Business Technology
    • Entertain­ment & Media
    • Financial Services & Investing
    • General Business
  • Science & Tech
    • Consumer Technology
    • Energy & Natural Resources
    • Environ­ment
    • Heavy Industry & Manufacturing
    • Telecomm­unications
  • Lifestyle & Health
    • Consumer Products & Retail
    • Entertain­ment & Media
    • Health
    • Sports
    • Travel
  • Policy & Public Interest
  • People & Culture
    • People & Culture
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • Explore Our Platform
  • Plan Campaigns
  • Create with AI
  • Distribute Press Releases
  • Amplify Content
  • All Products
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices
  • Send a Release
  • Client Login
  • Resources
  • Blog
  • Journalists
  • RSS

Visiongain Report Looks at Opportunities Within the $257bn Rare Disease Drugs Market

- Global Rare Disease Drugs Market Forecast 2019-2029

- Oncology, Metabolic Diseases, Neurologic Diseases, Haematology Diseases, Infectious Diseases, Specialty Pharmacies, Hospital Pharmacies, Retail Pharmacies

Visiongain Logo

News provided by

Visiongain

Oct 07, 2019, 05:00 ET

Share this article

Share toX

Share this article

Share toX

LONDON, Oct. 7, 2019 /PRNewswire/ -- The global rare disease drugs market is estimated to reach $257bn in 2024 and is expected to grow at a CAGR of 11.3% throughout the forecast period. In 2018, rare oncology diseases segment held 36% of share in the global rare disease drugs market.

How this report will benefit you
Read on to discover how you can exploit the future business opportunities emerging in this sector.

In this brand new 250-page report you will receive 145 charts– all unavailable elsewhere.

The 250-page report provides clear detailed insight into the global rare disease drugs market. Discover the key drivers and challenges affecting the market.

By ordering and reading Visiongain's brand-new report today you stay better informed and ready to act.

To request sample pages from this report please contact Sara Peerun at [email protected] or refer to our website: https://www.visiongain.com/report/global-rare-disease-drugs-market-forecast-2019-2029/#download_sampe_div

Report Scope

• Global Rare Disease Drugs Market forecasts from 2019-2029

• Revenue forecasts for the global rare disease drugs market by application from 2019-2029:
• Rare Oncology Diseases
• Rare Metabolic Diseases
• Rare Neurologic Diseases
• Rare Hematology Diseases
• Rare Infectious Diseases
• Other Rare Diseases

• Revenue forecasts for the global rare disease drugs market by distribution channel from 2019-2029:
• Specialty Pharmacies
• Hospital Pharmacies
• Retail Pharmacies

• Revenue forecasts for the global rare disease drugs market by drug from 2019-2029:
• Avonex
• Copaxone
• Gleevec
• Imbruvica
• MabThera/Rituxan
• Opdivo
• Rebif
• Revlimid
• Sprycel
• Tasigna
• Velcade
• Other Drugs

• Revenue forecasts for the rare disease drugs market by Regional and National Market from 2019-2029:
• North America (US, Canada)
• Europe (Germany, UK, France, Italy, Spain)
• Asia-Pacific (Japan, China, India, South Korea)
• RoW (Brazil, Mexico, South Africa, Russia)

• Profiles and discussion on the leading companies in the rare disease drugs market:
• AbbVie
• Bristol-Myers Squibb (BMS)
• Celgene
• Merck & Co., Inc.
• Novartis
• Pfizer
• Roche
• Sanofi
• Takeda
• Teva

• Rare disease drugs pipeline analysis covering rare oncology drugs, rare autoimmune disease drugs, blood-related rare disease drugs, rare genetic disease drugs and rare infectious disease drugs.

• SWOT Analysis and Porter's Five Forces analysis of the global rare disease drugs market

• Discussion on factors that drive and restrain the global rare disease drugs market as well as opportunities in this market.

• Key Questions Answered by this Report:
• What are the global revenue prospects for the period 2019 to 2029?
• What are the leading national market potentials from 2019 to 2029?
• How is the rare disease drugs market evolving?
• What is driving and restraining the rare disease drugs market?
• What are the market shares of each segment of the overall rare disease drugs market?
• How will main rare disease drugs submarket segments develop over the forecast period and how much revenue will these submarkets account for in 2029?
• How will the market shares for each rare disease drugs submarket develop from 2018 to 2029?
• Which therapies can succeed and what revenues could they generate to 2029?
• What will be the main commercial drivers for the market from 2018 to 2029?
• How will market shares of prominent national markets change from 2018, and which countries will lead the market in 2029, achieving highest revenues and fastest growth?
• How will that industry evolve between 2018 and 2029, especially in R&D?

To request a report overview of this report please contact Sara Peerun at [email protected] or refer to our website: https://www.visiongain.com/report/global-rare-disease-drugs-market-forecast-2019-2029/

Did you know that we also offer a report add-on service? Email [email protected] to discuss any customized research needs you may have.

Companies covered in the report include:

AB Science
AbbVie
Acceleron Pharma & Celgene
Acer Therapeutics
Actavis Generics
Actelion Pharmaceuticals
Actinium Pharmaceuticals
Adaptimmune
Aduro BioTech
Advanced Accelerator Applications
Advantagene
Advaxis
Advenchen Laboratories
Affimed Therapeutics & Merck
Agenus
Agios Pharmaceuticals
Akashi Therapeutics
Akcea Therapeutics
Alcobra
Alexion Pharmaceuticals
Alkeus Pharmaceuticals
Allergan
Alnylam Pharmaceuticals
Ambit Biosciences
AmerisourceBergen Corporation
Amgen
Amicus Therapeutics
Andarix Pharmaceuticals
Angimmune
Angiochem
AntiVirus Therapeutics
Applied Genetic Technologies
Araim Pharmaceuticals
Arch Biopartners
arGentis Pharmaceuticals
ARIAD Pharmaceuticals
ArmaGen Technologies
ARMGO Pharma
AROG Pharmaceuticals
ArQule
ArQule
Array BioPharma
Arrowhead Research
Astellas Pharma US
Astex Pharmaceuticals
AstraZeneca
ATARA Biotherapeutics
Atox Bio
aTyr Pharma
Baxalta
Bayer HealthCare Pharmaceuticals
Belrose Pharmaceuticals
BerGenBio
BioBlast Pharma
BioCryst Pharmaceuticals
Biodel
Biogen
BioInvent International
BioLineRx
BioMarin Pharmaceutical
BioNTech
Bio-Path Holdings
Biotest Pharmaceuticals
Blaze Bioscience
bluebird bio
Blueprint Medicines
Boehringer Ingelheim Pharmaceuticals
Bristol-Myers Squibb
Burzynski Research Institute
Caladrius Biosciences
Cancer Advances
Cancer Prevention Pharmaceutical
Capricor Therapeutics
Cardinal Health, Inc.
CASI Pharmaceuticals
Catabasis Pharmaceuticals
Cavion
Celator Pharmaceuticals
Celgene Corporation
Cell Medica
Cell Therapeutics
Cellectar Biosciences
CEL-SCI
Celsion
Celtaxsys
Cempra Pharmaceuticals
CerRx
Cerulean Pharma
ChemoCentryx
Chugai Pharma
Cidara Therapeutics
Cleave Biosciences
Clementia Pharmaceuticals
Clinuvel
Clovis Oncology
Confluence Pharmaceuticals
Corbus Pharmaceuticals
Cornerstone Pharmaceuticals
Cortice Biosciences
Critical Outcome Technologies
Curis
Cyclacel
CymaBay Therapeutics
CytRx
Daiichi Sankyo
Deciphera Pharmaceuticals
Delcath Systems
DelMar Pharmaceuticals
Diffusion Pharmaceuticals
Dimension Therapeutics
Diurnal
DNAtrix
Eddingpharm
Edimer Pharmaceuticals
Edison Pharmaceuticals
Eiger Biopharmaceuticals
Eisai
Eleison Pharmaceuticals
Eli Lilly
EMD Serono & Pfizer
Emergent BioSolutions
Emmaus Medical
Epitopoietic Research
Epizyme
Epizyme
EryDel
Escala Therapeutics
Essentialis
Five Prime Therapeutics
Fortress Biotech
Gamida Cell
Gem Pharmaceuticals
Gen Sight Biologics
Genentech
GenSpera
Genzyme
Gilead Sciences
GlaxoSmithKline
Gliknik
Global Blood Therapeutics
GlycoMimetics
Golden Biotechnology
Gradalis
Grifols Therapeutics
GW Pharma
Halozyme Therapeutics
Hanmi
Hoffmann-La Roche Ltd
Horizon Pharma
Idera Pharmaceuticals
Ignyta
Immatics Biotechnologies
Immune Design
Immune Pharmaceuticals
Immune Response BioPharma
Immune Therapeutics
ImmunoCellular Therapeutics
ImmunoGen
Immunomedics
Immunovaccine Technologies
Incyte
Infinity Pharmaceuticals
InnoPharma
Insmed
Insys Therapeutics
Ionis Pharmaceuticals
Ionis Pharmaceuticals
Ipsen Biopharmaceuticals
IRX Therapeutics
Janssen Biotech
jCyte
Juno Therapeutics
Karyopharm Therapeutics
Kevelt
Kyowa Kirin USA
LeafBio
Lexicon Pharmaceuticals
Lion Biotechnologies
LipimetiX Development
MabVax Therapeutics
Marathon Pharmaceuticals
Marina Biotech
Mast Therapeutics
McKesson Corporation
MedImmune
MEI Pharma
Merck & Co., Inc
Millendo Therapeutics
Millennium Pharmaceuticals
Milo Biotechnology
Minneamrita Therapeutics
Mirati Therapeutics
Momenta Pharmaceuticals
MorphoSys
Nektar Therapeutics
NeOnc Technologies
Neuren Pharmaceuticals
Neurolixis
Neurotech USA
NGM Biopharmaceuticals
NightstaRx
Nivalis Therapeutics
NKT Therapeutics
Novartis Pharmaceuticals
Novo Nordisk
Novoteris
Ocata Therapeutics
Omeros
On Target Laboratories
Oncolix
Oncolytics Biotech
OncoMed Pharmaceuticals
OncoMed Pharmaceuticals & GlaxoSmithKline
Onconova Therapeutics
OncoPep
Oncopeptides
OPKO Biologics
OSE Pharma
Otsuka Pharmaceutical
OXiGENE
Patagonia Pharmaceuticals
Peregrine Pharmaceuticals
Pfizer Inc.
Pharmacyclics
PharmaCyte Biotech
PharmaEssentia, Corporation
PharmaMar USA
Plexxikon
PNP Therapeutics
Polaris Pharmaceuticals
Polynoma
Prana Biotechnology
Precision Biologics
Progenics Pharmaceuticals
Prolong Pharmaceuticals
Promedior
ProMetic Biotherapeutics
ProNAi Therapeutics
ProQR Therapeutics
Protalex
Provectus Pharmaceuticals
PTC Therapeutics
QLT
Quest PharmaTech
Qurient
Raptor Pharmaceutical
Rebiotx
Regeneron Pharmaceuticals
Regulus Therapeutics & Sanofi US
Retrophin
RetroSense Therapeutics
ReveraGen Biopharma
Rexahn Pharmaceuticals
Rhythm Metabolics
Rigel Pharmaceuticals
River Vision
Roche
Sanofi S. A.
Santhera Pharmaceuticals
Sarepta Therapeutics
Savara Pharmaceuticals
Seattle Genetics
Selexys Pharmaceuticals
SELLAS Life Sciences
Sequella
Seres Health
Shire plc
SIGA Technologies
Sigma-Tau Pharmaceuticals
SillaJen Biotherapeutics
Soligenix
Soricimed Biopharma
Spark Therapeutics
StemcentRx
Stemline Therapeutics
Sun BioPharma
Sun Pharmaceuticals
Sunesis Pharmaceuticals
Takeda Pharmaceuticals
Tapimmune
Tarix Orphan
TESARO
TetraLogic Pharmaceuticals
Teva Pharmaceutical
TG Therapeutics
Tiziana Life Sciences
Tocagen
Tolero Pharmaceuticals
Tracon Pharmaceuticals
TransDerm
Triphase Research & Development
Triphase Research and Development
Ultragenyx Pharmaceutical
Ultragenyx Pharmaceutical
uniQure
UroGen
Vascular Biogenics
VentiRx Pharmaceuticals
Verastem
Vertex Pharmaceuticals
Viamet Pharmaceuticals
Vicus Therapeutics
Viralytics
Viventia Biotech
VivoLux
Vtesse
Wilson Therapeutics
Xeris Pharmaceuticals
XOMA
Ziopharm Oncology
Zogenix
Zywie

To see a report overview please e-mail Sara Peerun on [email protected]

Related reports:

Global Macular Degeneration (AMD) and Other Retinal Diseases Drugs Industry and Market 2019-2029

Global OTC Pharmaceutical Market Forecast 2019-2029

Global Stem Cell Technologies and Applications Market 2019-2029

Global Inflammatory Bowel Diseases (IBD) Drug Market Forecast 2019-2029

Orphan Drugs Market Report 2018-2028 

SOURCE Visiongain

21%

more press release views with 
Request a Demo

Modal title

Contact PR Newswire

  • Call PR Newswire at 888-776-0942
    from 8 AM - 9 PM ET
  • Chat with an Expert
  • General Inquiries
  • Editorial Bureaus
  • Partnerships
  • Media Inquiries
  • Worldwide Offices

Products

  • For Marketers
  • For Public Relations
  • For IR & Compliance
  • For Agency
  • All Products

About

  • About PR Newswire
  • About Cision
  • Become a Publishing Partner
  • Become a Channel Partner
  • Careers
  • Accessibility Statement
  • APAC
  • APAC - Simplified Chinese
  • APAC - Traditional Chinese
  • Brazil
  • Canada
  • Czech
  • Denmark
  • Finland
  • France
  • Germany
  • India
  • Indonesia
  • Israel
  • Italy
  • Japan
  • Korea
  • Mexico
  • Middle East
  • Middle East - Arabic
  • Netherlands
  • Norway
  • Poland
  • Portugal
  • Russia
  • Slovakia
  • Spain
  • Sweden
  • United Kingdom
  • Vietnam

My Services

  • All New Releases
  • Platform Login
  • ProfNet
  • Data Privacy

Do not sell or share my personal information:

  • Submit via [email protected] 
  • Call Privacy toll-free: 877-297-8921

Contact PR Newswire

Products

About

My Services
  • All News Releases
  • Platform Login
  • ProfNet
Call PR Newswire at
888-776-0942
  • Terms of Use
  • Privacy Policy
  • Information Security Policy
  • Site Map
  • RSS
  • Cookies
Copyright © 2025 Cision US Inc.