Search Results

Displaying Results 3926-3950 of 7521 "'RARE'"

Mar 30, 2026, 10:14 ET CurePSP Convenes Bipartisan Congressional Briefing to Advance PSP, CBD and MSA Research

me, it can happen to them or to someone they love.""Hearing my dear friend and mentor Jennifer Wexton's story reminds us that while PSP may be rare, the need for answers is urgent," said Rep. Subramanyam. "Thank you to CurePSP for pushing for change on Capitol Hill."About CurePSPCurePSP

More news about: CurePSP, Inc.


Mar 30, 2026, 10:00 ET A New Era at Jeptha Creed: Expanded Distillery Experiences Arrive In 2026

dive.Opening on March 1st, 2026, the all-new Single Barrel Thieving experience invites guests deeper into the heart of Jeptha Creed, offering a rare behind-the-scenes look at the art of single-barrel selection. Visitors will gain firsthand insight into the Nethery family philosophy and how Joyce

More news about: Jeptha Creed Distillery


Mar 30, 2026, 09:35 ET Hengrui Pharma and Braveheart Bio Announce Positive Phase 2 Results with HRS/BHB-1893 in Obstructive Hypertrophic Cardiomyopathy

American College of Cardiology's Annual Scientific Session & Expo.About Hypertrophic CardiomyopathyHCM is among the most common rare diseases, affecting approximately 1 in 500 individuals in the United States. HCM can lead to heart failure, stroke or sudden cardiac death, including

More news about: Braveheart Bio


Mar 30, 2026, 09:33 ET Real Estate Expert Justus Smith of Keystone Highlights North Florida's Appeal for HelloNation

feel while offering larger lots and more privacy. For families, retirees, and remote professionals, that combination of affordability and open space is rare in Florida's competitive market. The HelloNation article notes that lower home prices do not mean a compromise in quality of life. Instead, they provide

More news about: HelloNation


Mar 30, 2026, 09:00 ET Charlie Health Names New Chief Technology Officer to Accelerate Technology and AI Strategy

making intentional investments in the technology that powers our care model," said Carter Barnhart, CEO and Co-Founder at Charlie Health. "Ashok brings a rare combination of technical depth and healthcare experience, and his leadership will be instrumental in helping us accelerate innovation, strengthen our

More news about: Charlie Health


Mar 30, 2026, 08:58 ET Jeffrey Modell Foundation to Host NIH Immunology Leader for World Primary Immunodeficiency Week

therapeutic modulation in immune mediated disease. She has dedicated her academic career to translational research and clinical care of patients with rare immunologic disease through the development of multidisciplinary translational programs such as the TCH Immune Disorder Clinic Network, which connects

More news about: Jeffrey Modell Foundation


Mar 30, 2026, 08:32 ET Once Upon a Coconut Promotes Matt Merson to President

has been a force for this organization from the moment he walked in the door," said John Chiorando, CEO of Once Upon a Coconut. "He brings the rare combination of big-brand experience and founder-level urgency, and he's earned every bit of this. Promoting Matt to President is the right call for

More news about: Once Upon A Coconut


Mar 30, 2026, 08:00 ET Calliditas Therapeutics AB to Present Exploratory Biomarker and Post-Hoc NefIgArd Analyses at the World Congress of Nephrology

nephropathy.About Primary Immunoglobulin A NephropathyPrimary immunoglobulin A nephropathy (IgA nephropathy or IgAN or Berger's Disease) is a rare, progressive, chronic immune-mediated disease that attacks the kidneys and occurs when galactose-deficient IgA1 is recognized by autoantibodies, creating

More news about: Calliditas Therapeutics


Mar 30, 2026, 07:43 ET CELEBRATING 25 YEARS AND BEYOND OF LIFE AFTER ORGAN TRANSPLANTATION AT THE NATIONAL UNIVERSITY CENTRE FOR ORGAN TRANSPLANTATION

she had a liver transplant in 1996, making her the youngest liver transplant recipient in Singapore at the time. She was born with biliary atresia, a rare condition affecting newborns where the bile duct is blocked or did not develop properly.Now in her early 30s, she recounts: "Receiving a liver

More news about: National University Hospital (NUH)


Mar 30, 2026, 07:06 ET New Analyses: EPA Consistently Fails to Warn Public of Pesticide Cancer Risks

acquired by Bayer, is seeking substantial immunity from future lawsuits brought by Americans who used glyphosate-based products like Roundup and contracted rare cancers that numerous studies have linked to the pesticide. The case hinges on whether the EPA has sole authority to implement pesticide label warnings.Both

More news about: The Center For Food Safety


Mar 30, 2026, 07:00 ET Nanoscope Therapeutics Receives Orphan Drug Designation in Saudi Arabia for MCO-010, Expands Global Regulatory Leadership in Vision Restoration

Agency (EMA), spanning a broad range of IRDs, supporting a disease-agnostic regulatory strategy across multiple indications.IRDs are a group of rare, progressive diseases that lead to severe vision loss or blindness and currently lack treatment options. By progressing regulatory pathways across

More news about: Nanoscope Therapeutics


Mar 30, 2026, 06:59 ET Cryogenic Vaporizer Market worth $0.72 billion by 2031 - Exclusive Report by MarketsandMarkets™

increasingly used in high-value and precise applications. Electronics manufacturing, space research, and scientific laboratories now use helium, hydrogen, and rare gas mixtures to maintain exact temperature control and deliver ultra-pure gas. The rising demand for semiconductors and advanced electronics drives

More news about: MarketsandMarkets


Mar 30, 2026, 06:00 ET Thesis Gold & Silver Identifies Two Distinct Porphyry Targets on the Lawyers-Ranch Project

identification of two porphyry systems at different levels of exposure highlights the district-scale potential emerging at Ranch. Ranch East provides a rare window into deeper levels of a porphyry system, while Ranch preserves the upper lithocap portion of a similar system. Together, these observations significantly

More news about: Thesis Gold & Silver


Mar 30, 2026, 03:41 ET Ultragenyx Pharmaceutical Inc. Sued for Securities Law Violations - Contact the DJS Law Group to Discuss Your Rights - RARE

Inc. ("Ultragenyx" or "the Company") (NASDAQ: RARE) for violations of §§10(b) and 20(a) of the Securities Exchange Act of 1934 and Rule 10b-5 promulgated thereunder by the U.S. Securities and Exchange Commission. Shareholders who purchased shares of RARE during the class period listed are encouraged

More news about: DJS Law Group LLP


Mar 30, 2026, 02:35 ET RARE Investors Have Opportunity to Lead Ultragenyx Pharmaceutical Inc. Securities Fraud Lawsuit with the Schall Law Firm

rights litigation firm, reminds investors of a class action lawsuit against Ultragenyx Pharmaceutical Inc. ("Ultragenyx" or "the Company") (NASDAQ: RARE) for violations of §§10(b) and 20(a) of the Securities Exchange Act of 1934 and Rule 10b-5 promulgated thereunder by the U.S. Securities and Exchange

More news about: The Schall Law Firm


Mar 30, 2026, 02:23 ET EMA validates indication extension application for Tryngolza® (olezarsen) for the treatment of severe hypertriglyceridemia (sHTG)

Sobi®Sobi® is a global biopharma company unlocking the potential of breakthrough innovations, transforming everyday life for people living with rare diseases. Sobi has approximately 1,900 employees across Europe, North America, the Middle East, Asia and Australia. In 2025 revenue amounted to SEK

More news about: Swedish Orphan Biovitrum AB


Mar 29, 2026, 08:57 ET n6 Launches icon16™, Expanding AutoNorm™ Adaptive Amplification to Lower-Throughput NGS Workflows

format, purpose-built for labs running NGS at lower throughput, including single-cell RNA sequencing, spatial transcriptomics, cfDNA and MRD assays, rare disease sequencing, and other workflows where researchers typically process smaller batches of samples.In many low-input workflows such as single-cell

More news about: n6


Mar 29, 2026, 08:14 ET RARE DEADLINE ALERT: Faruqi & Faruqi, LLP Reminds Ultragenyx Investors of Securities Class Action Deadline on April 6, 2026

leading national securities law firm, is investigating potential claims against Ultragenyx Pharmaceutical Inc ("Ultragenyx" or the "Company") (NASDAQ: RARE) and reminds investors of the April 6, 2026 deadline to seek the role of lead plaintiff in a federal securities class action that has been filed

More news about: Faruqi & Faruqi, LLP


Mar 29, 2026, 04:18 ET Inside China's wildest cave basketball court

and chanting, as the sound of bouncing basketballs echoed through the towering limestone chamber.The game offered visiting content creators a rare opportunity to experience China's grassroots basketball phenomenon known as "Village BA", where community spirit, local pride and a passion for the

More news about: chinadaily.com.cn


Mar 28, 2026, 16:45 ET REPATHA® CUTS RISK OF FIRST MAJOR CARDIOVASCULAR EVENTS BY 31% IN HIGH-RISK PATIENTS WITHOUT KNOWN SIGNIFICANT ATHEROSCLEROSIS

what is known today. Amgen is advancing a broad and deep pipeline and portfolio of medicines to treat cancer, heart disease, inflammatory conditions, rare diseases and obesity and obesity-related conditions.Amgen has been

More news about: Amgen


Mar 28, 2026, 14:39 ET Das Critical Path Institute startet die Initiative „One to Millions", um die Zukunft der personalisierten Medizin weltweit neu zu gestalten

Um diese Lücke zu schließen, fördert One to Millions das „Plausible Mechanism Framework" und die „Rare Disease Evidence Principles" der US-amerikanischen Food and Drug Administration (FDA), indem es die zentralisierte, behördlich anerkannte Datenplattform

More news about: Critical Path Institute


Mar 27, 2026, 22:46 ET Ultragenyx Pharmaceutical Inc. Notice of April 6, 2026 Application Deadline for Class Action Lawsuit - Contact Lewis Kahn, Esq. at Kahn Swick & Foti, LLC, Before Application Deadline

Ultragenyx Pharmaceutical Inc. ("Ultragenyx" or the "Company") (NasdaqGS: RARE) of a class action securities lawsuit.

More news about: Kahn Swick & Foti, LLC


Mar 27, 2026, 14:19 ET Boris Becker's 1989 U.S. Open Champion Trophy Up For Auction, $350,000+ Expected

Men's Singles / Boris Becker / 1989." Grand Slam trophies virtually never leave the possession of the player who won them, making this an incredibly rare opportunity. This trophy was previously exhibited at the International Tennis Hall of Fame in Newport, Rhode Island, where it was displayed on loan

More news about: Prestige Memorabilia


Mar 27, 2026, 14:05 ET Boris Becker's 1989 U.S. Open Champion Trophy Up For Auction, $350,000+ Expected

Men's Singles / Boris Becker / 1989." Grand Slam trophies virtually never leave the possession of the player who won them, making this an incredibly rare opportunity. This trophy was previously exhibited at the International Tennis Hall of Fame in Newport, Rhode Island, where it was displayed on loan

More news about: Prestige Memorabilia


Mar 27, 2026, 13:20 ET Critical Path Institute uruchamia inicjatywę „Od jednego do milionów", aby zmienić przyszłość medycyny spersonalizowanej w skali globalnej

koncepcję Plausible Mechanism Framework opracowaną przez amerykańską Agencję Żywności i Leków (FDA) oraz zasady dotyczące dowodów w chorobach rzadkich (Rare Disease Evidence Principles), wykorzystując scentralizowaną platformę danych C-Path o jakości spełniającą wymogi regulacyjne do wspierania gromadzenia

More news about: Critical Path Institute


Making a selection with these dropdown will cause content on this page to change. News search result will update as each option is selected.